| Phase 1/2 | 2 |
| NCT ID | Title | Condition | Status | Updated |
|---|---|---|---|---|
| Phase 1/2 | ||||
| NCT04693598 | Gene Transfer Clinical Trial for Krabbe Disease | Krabbe Disease | Active, Not Recruiting | 2026-06-02 |
| NCT05739643 | Gene Transfer Clinical Trial for Infantile and Late Infantile Krabbe Disease Treated… | Krabbe Disease | Active, Not Recruiting | 2025-11-20 |