| Phase 1/2 | 1 | |
| Phase 3 | 1 |
| NCT ID | Title | Condition | Status | Updated |
|---|---|---|---|---|
| Phase 3 | ||||
| NCT05878860 | ATSN-201 Gene Therapy in RS1-Associated X-linked Retinoschisis | X-linked Retinoschisis | Recruiting | 2026-09-29 |
| Phase 1/2 | ||||
| NCT03920007 | Study of Subretinally Injected ATSN-101 Administered in Patients With Leber Congenital… | Leber Congenital Amaurosis | Active, Not Recruiting | 2026-08-03 |