| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 3 | |||
| NCT07054515 | A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in… | Niemann-Pick Type C Disease | Recruiting |
| NCT07082543 | A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in… | Gangliosidoses, GM2 | Recruiting |
| NCT07082725 | A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in… | Niemann-Pick Type C Disease | Recruiting |
| Phase 2 | |||
| NCT07399704 | A Study to Evaluate the Safety and Efficacy of Nizubaglustat (AZ-3102) in Patients With… | GM2 Gangliosidosis | Recruiting |