Also listed under Abnormalities, Multiple, Brain Diseases, Metabolic, Inborn, Kidney Diseases, Peroxisomal Disorders
Trials about this condition or a more specific one, based on ClinicalTrials.gov's categories.
Top sponsors: McGill University Health Centre/Research Institute of the McGill University Health Centre (2) · Children's Hospital of Philadelphia (1) · Masonic Cancer Center, University of Minnesota (1) · Mirum Pharmaceuticals, Inc. (1)
Data updated daily from ClinicalTrials.gov.