Also listed under Brain Diseases, Metabolic, Inborn
Trials about this condition or a more specific one, based on ClinicalTrials.gov's categories.
Top sponsors: BioMarin Pharmaceutical (6) · Otsuka Pharmaceutical Development & Commercialization, Inc. (4) · Central Hospital, Nancy, France (2) · Emory University (2) · Nutricia UK Ltd (2)
Data updated daily from ClinicalTrials.gov.