Also listed under Abnormalities, Multiple, Chromosome Disorders, Imprinting Disorders
Trials about this condition or a more specific one, based on ClinicalTrials.gov's categories.
Top sponsors: Ionis Pharmaceuticals, Inc. (3) · Ultragenyx Pharmaceutical Inc (3) · RTI International (2) · Assistance Publique - Hôpitaux de Paris (1) · Boston Children's Hospital (1)
Data updated daily from ClinicalTrials.gov.